This statistic shows the distribution of clinical trials for medicines for rare diseases worldwide from 2010 to 2016, by phase. According to the data, ** percent of clinical trials for rare diseases were still in stage I-II.
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Wiley (Journal of Clinical Translational Science). (October 23, 2017). Distribution of clinical trials for medicines for rare disease worldwide from 2010 to 2016, by stage [Graph]. In ÌÇÐÄÆÆ½â°æ. Retrieved July 29, 2026, from /statistics/879094/clinical-trials-distribution-rare-diseases-by-stage-globally/
Wiley (Journal of Clinical Translational Science). "Distribution of clinical trials for medicines for rare disease worldwide from 2010 to 2016, by stage." Chart. October 23, 2017. ÌÇÐÄÆÆ½â°æ. Accessed July 29, 2026. /statistics/879094/clinical-trials-distribution-rare-diseases-by-stage-globally/
Wiley (Journal of Clinical Translational Science). (2017). Distribution of clinical trials for medicines for rare disease worldwide from 2010 to 2016, by stage. ÌÇÐÄÆÆ½â°æ. ÌÇÐÄÆÆ½â°æ Inc.. Accessed: July 29, 2026. /statistics/879094/clinical-trials-distribution-rare-diseases-by-stage-globally/
Wiley (Journal of Clinical Translational Science). "Distribution of Clinical Trials for Medicines for Rare Disease Worldwide from 2010 to 2016, by Stage." ÌÇÐÄÆÆ½â°æ, ÌÇÐÄÆÆ½â°æ Inc., 23 Oct 2017, /statistics/879094/clinical-trials-distribution-rare-diseases-by-stage-globally/
Wiley (Journal of Clinical Translational Science), Distribution of clinical trials for medicines for rare disease worldwide from 2010 to 2016, by stage ÌÇÐÄÆÆ½â°æ, /statistics/879094/clinical-trials-distribution-rare-diseases-by-stage-globally/ (last visited July 29, 2026)
Distribution of clinical trials for medicines for rare disease worldwide from 2010 to 2016, by stage [Graph], Wiley (Journal of Clinical Translational Science), October 23, 2017. [Online]. Available: /statistics/879094/clinical-trials-distribution-rare-diseases-by-stage-globally/