This statistic shows the distribution of clinical trials worldwide for rare diseases from 2010 to 2016, by disease type. According to the data, ** percent of clinical trials for rare diseases were focused on rare neoplastic diseases. Neoplastic diseases are diseases of unusual growth, mainly cancers, but could also include benign growths as well.
Profit from the additional features of your individual account
Currently, you are using a shared account. To use individual functions (e.g., mark statistics as favourites, set
statistic alerts) please log in with your personal account.
If you are an admin, please authenticate by logging in again.
Learn more about how ÌÇÐÄÆÆ½â°æ can support your business.
Wiley (Journal of Clinical Translational Science). (October 23, 2017). Distribution of global clinical trials for medicines for rare diseases from 2010 to 2016, by type of disease [Graph]. In ÌÇÐÄÆÆ½â°æ. Retrieved July 29, 2026, from /statistics/879057/clinical-trials-rare-disease-distribution-by-disease-type/
Wiley (Journal of Clinical Translational Science). "Distribution of global clinical trials for medicines for rare diseases from 2010 to 2016, by type of disease." Chart. October 23, 2017. ÌÇÐÄÆÆ½â°æ. Accessed July 29, 2026. /statistics/879057/clinical-trials-rare-disease-distribution-by-disease-type/
Wiley (Journal of Clinical Translational Science). (2017). Distribution of global clinical trials for medicines for rare diseases from 2010 to 2016, by type of disease. ÌÇÐÄÆÆ½â°æ. ÌÇÐÄÆÆ½â°æ Inc.. Accessed: July 29, 2026. /statistics/879057/clinical-trials-rare-disease-distribution-by-disease-type/
Wiley (Journal of Clinical Translational Science). "Distribution of Global Clinical Trials for Medicines for Rare Diseases from 2010 to 2016, by Type of Disease." ÌÇÐÄÆÆ½â°æ, ÌÇÐÄÆÆ½â°æ Inc., 23 Oct 2017, /statistics/879057/clinical-trials-rare-disease-distribution-by-disease-type/
Wiley (Journal of Clinical Translational Science), Distribution of global clinical trials for medicines for rare diseases from 2010 to 2016, by type of disease ÌÇÐÄÆÆ½â°æ, /statistics/879057/clinical-trials-rare-disease-distribution-by-disease-type/ (last visited July 29, 2026)
Distribution of global clinical trials for medicines for rare diseases from 2010 to 2016, by type of disease [Graph], Wiley (Journal of Clinical Translational Science), October 23, 2017. [Online]. Available: /statistics/879057/clinical-trials-rare-disease-distribution-by-disease-type/